Review Articles Exploration of New Contrasts, Targets, and MR Imaging and Spectroscopy Techniques for Neuromuscular Disease – Open Access Strijkers, Gustav J. | Araujo, Ericky C.A. | Azzabou, Noura | Bendahan, David | Blamire, Andrew | Burakiewicz, Jedrek | Carlier, Pierre G. | Damon, Bruce | Deligianni, Xeni | Froeling, Martijn | Heerschap, Arend | Hollingsworth, Kieren G. | Hooijmans, Melissa T. | Karampinos, Dimitrios C. | et al. Management of Adrenal Insufficiency Risk After Long-term Systemic Glucocorticoid Therapy in Duchenne Muscular Dystrophy: Clinical Practice Recommendations – Open Access Bowden, Sasigarn A. | Connolly, Anne M. | Kinnett, Kathi | Zeitler, Philip S. Research Articles Phase 1 Study of Edasalonexent (CAT-1004), an Oral NF- κB Inhibitor, in Pediatric Patients with Duchenne Muscular Dystrophy – Open Access Finanger, Erika | Vandenborne, Krista | Finkel, Richard S. | Lee Sweeney, H. | Tennekoon, Gihan | Yum, Sabrina | Mancini, Maria | Bista, Pradeep | Nichols, Andrew | Liu, Hanlan | Fretzen, Angelika | Donovan, Joanne M. Echographic Assessment of Diaphragmatic Function in Duchenne Muscular Dystrophy from Childhood to Adulthood Fayssoil, Abdallah | Chaffaut, Cendrine | Ogna, Adam | Stojkovic, Tanya | Lamothe, Laure | Mompoint, Dominique | Meng, Paris | Prigent, Helene | Clair, Bernard | Behin, Anthony | Laforet, Pascal | Bassez, Guillaume | Carlier, Robert | Orlikowski, David | Amthor, Helge | Quijano Roy, Susana | Crenn, Pascal | Chevret, Sylvie | Eymard, Bruno | Lofaso, Frederic | Annane, Djillali Increased Blood Pressure and Body Mass Index as Potential Modifiable Factors in The Progression of Myocardial Dysfunction in Duchenne Muscular Dystrophy van de Velde, Nienke Marije | Roest, Arno Anne Willem | van Zwet, Erik Willem | Niks, Erik Harmen Lower Extremity Functional Outcome Measures in Duchenne Muscular Dystrophy-A Delphi Survey Senesac, Claudia R. | Lott, Donovan J. | Willcocks, Rebecca J. | Duong, Tina | Smith, Barbara K. Pattern of Habitual Physical Exercise in Myasthenia Gravis Patients O’Connor, Laura | Westerberg, Elisabet | Punga, Anna Rostedt Muscle Strength and Aerobic Capacity in Patients with CIDP One Year after Participation in an Exercise Trial Markvardsen, Lars K. | Carstens, Anne-Kathrine R. | Knak, Kirsten L. | Overgaard, Kristian | Vissing, John | Andersen, Henning Responsiveness to Change of 5-point MRC scale, Endurance and Functional Evaluation for Assessing Myositis in Daily Clinical Practice Landon-Cardinal, Océane | Devilliers, Hervé | Chavarot, Nathalie | Mariampillai, Kuberaka | Rigolet, Aude | Hervier, Baptiste | Allenbach, Yves | Benveniste, Olivier Perceived Fatigue in Spinal Muscular Atrophy: A Pilot Study Dunaway Young, Sally | Montes, Jacqueline | Kramer, Samantha S. | Podwika, Bernadette | Rao, Ashwini K. | De Vivo, Darryl C. Perspectives on Spinraza (Nusinersen) Treatment Study: Views of Individuals and Parents of Children Diagnosed with Spinal Muscular Atrophy Pacione, Michelle | Siskind, Carly E. | Day, John W. | Tabor, Holly K. Reliability and Validity of Self-Report Questionnaires as Indicators of Fatigue in RYR1-Related Disorders Kuo, Anna | Todd, Joshua J. | Witherspoon, Jessica W. | Lawal, Tokunbor A. | Elliott, Jeffery | Chrismer, Irene C. | Shelton, Monique O. | Razaqyar, Muslima S. | Jain, Minal S. | Vasavada, Ruhi | Waite, Melissa | Drinkard, Bart | Michael, Darren | Richarte, Alicia | Bönnemann, Carsten G. | Meilleur, Katherine G. Homozygous Nonsense Mutation p.Q274X in TRIM63 (MuRF1) in a Patient with Mild Skeletal Myopathy and Cardiac Hypertrophy Jokela, Manu | Baumann, Peter | Huovinen, Sanna | Penttilä, Sini | Udd, Bjarne Other Content Report of a TREAT-NMD/World Duchenne Organisation Meeting on Dystrophin Quantification Methodology – Open Access Aartsma-Rus, Annemieke | Morgan, Jennifer | Lonkar, Pallavi | Neubert, Hendrik | Owens, Jane | Binks, Michael | Montolio, Marisol | Phadke, Rahul | Datson, Nicole | Van Deutekom, Judith | Morris, Glenn E. | Rao, V. Ashutosh | Hoffman, Eric P. | Muntoni, Francesco | Arechavala-Gomeza, Virginia | on behalf of the workshop participants The Position of Neuromuscular Patients in Shared Decision Making. Report from the 235th ENMC Workshop: Milan, Italy, January 19-20, 2018 – Openly Available (view press release here) Lochmüller, Hanns | Ambrosini, Anna | van Engelen, Baziel | Hansson, Mats | Tibben, Aad | Breukel, Alexandra | Sterrenburg, Ellen | Schrijvers, Guus | Meijer, Ingeborg | Padberg, George | Peay, Holly | Monaco, Lucia | Snape, Mike | Lennox, Anne | Mazzone, Elena | Bere, Nathalie | de Lemus, Mencia | Landfeldt, Erik | Willmann, Raffaella | behalf of the 235th ENMC workshop study group Myotubular Trust - 2019 Call for Projects (Open to International Applications) – Openly Available Announcement | Most Read JND Articles in January 2019 Listing articles published only in 2018 and 2019 so you can read the most popular recent content Current Classification and Management of Inflammatory Myopathies – Open Access (Review Article in Vol.5, Iss.2, 2018) Schmidt, Jens Treatment Algorithm for Infants Diagnosed with Spinal Muscular Atrophy through Newborn Screening – Open Access (Research Article in Vol.5, Iss.2, 2018) Glascock, Jacqueline | Sampson, Jacinda | Haidet-Phillips, Amanda | Connolly, Anne | Darras, Basil | Day, John | Finkel, Richard | Howell, R. Rodney | Klinger, Katherine | Kuntz, Nancy | Prior, Thomas | Shieh, Perry B. | Crawford, Thomas O. | Kerr, Douglas | Jarecki, Jill Evaluation of Children with SMA Type 1 Under Treatment with Nusinersen within the Expanded Access Program in Germany – Open Access (Research Article in Vol.5, Iss.2, 2018) Pechmann, Astrid | Langer, Thorsten | Schorling, David | Stein, Sabine | Vogt, Sibylle | Schara, Ulrike | Kölbel, Heike | Schwartz, Oliver | Hahn, Andreas | Giese, Kerstin | Johannsen, Jessika | Denecke, Jonas | Weiß, Claudia | Theophil, Manuela | Kirschner, Janbernd Diaphragm: Pathophysiology and Ultrasound Imaging in Neuromuscular Disorders – Open Access (Review Article in Vol.5, Iss.1, 2018) Fayssoil, Abdallah | Behin, Anthony | Ogna, Adam | Mompoint, Dominique | Amthor, Helge | Clair, Bernard | Laforet, Pascal | Mansart, Arnaud | Prigent, Helene | Orlikowski, David | Stojkovic, Tanya | Vinit, Stéphane | Carlier, Robert | Eymard, Bruno | Lofaso, Frederic | Annane, Djillali Report of a TREAT-NMD/World Duchenne Organisation Meeting on Dystrophin Quantification Methodology – Open Access (Meeting Report in Vol.6, Iss.1, 2019) Aartsma-Rus, Annemieke | Morgan, Jennifer | Lonkar, Pallavi | Neubert, Hendrik | Owens, Jane | Binks, Michael | Montolio, Marisol | Phadke, Rahul | Datson, Nicole | Van Deutekom, Judith | Morris, Glenn E. | Rao, V. Ashutosh | Hoffman, Eric P. | Muntoni, Francesco | Arechavala-Gomeza, Virginia | on behalf of the workshop participants | July 1–5, 2019 | Leiden, the Netherlands The 2019 Neuromuscular Translational Summer School will be taking place from 1st to 5th July at Leiden University Medical Center in the Netherlands. The aim of the school is to facilitate the clinical development of therapies for NMDs, to educate clinicians and researchers working in the NMD field on aspects relevant for translational therapy development and to outline and showcase how networks like EURO-NMD and TREAT-NMD facilitate therapy development. Further details and registration information are available via the EURO-NMD website. | December 9–11, 2019 | Leiden, the Netherlands | Save the Date! The TREAT-NMD Alliance will hold its next international conference in Leiden, the Netherlands in December 2019. The conference will provide an engaging platform for clinical specialists, academics, patients and carers, advocacy organisations and Industry professionals to share progress and lessons learned in the area of translational medicine in inherited neuromuscular diseases and plan for the delivery of future therapies to patients. Further details will be released via the conference website in due course. | Sign Ups & Social Media Help Spread the News of JND! If you know of any colleagues or fellow researchers who are not yet signed up to receive the newsletter, we invite you to share this mailing with them. Click on the sign-up link at the bottom of this email or access here. If you are not yet interacting with JND on social media, why not take the time today to follow us on Twitter and find us on Facebook? 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